Experimental gene therapy for giant axonal neuropathy shows promise in NIH clinical trial
Experimental gene therapy for giant axonal neuropathy shows promise in NIH clinical trial Treatment for…
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Drug shows promise for slowing progression of rare, painful genetic disease
Drug shows promise for slowing progression of rare, painful genetic disease NIH-supported clinical trial could…
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Benign nail condition linked to rare syndrome that greatly increases cancer risk
Benign nail condition linked to rare syndrome that greatly increases cancer risk NIH researchers suggest…
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Existing drug shows promise as treatment for rare genetic disorder
Existing drug shows promise as treatment for rare genetic disorder NIH researchers find new pathways…